Day 2 Agenda

PFIC Network Scientific Conference Day 2 Agenda

April 29-30 in Pittsburgh, PA and virtual
*Agenda is subject to changes*

Day 2:

8:30 – 9:00

Saturday, April 30th

PFIC Network Organization & Community Updates
Emily Ventura, Executive Director of PFIC Network & Co-Founder

Scientific Presentations: Block #2
20 Minute Presentations + 10 Minute Q&A

Moderated by Dr. James Squires, Children’s Hospital Pittsburgh

9:00 – 9:30

9:30 – 10:00

10:00 – 10:30

10:30 – 11:00

11:00 – 11:30

11:30 – 12:00

Roundtable Discussions

12:00 – 1:30

1:30 – 2:00

5:00

6:00

Ileal Bypass in PFIC
Dr. Piotr Czubkowski, The Children’s Memorial Institute, Poland (in person)

Role of Liver Transplant in Tight Junction Protein 2 Deficiency
Dr. Dr Menon, Dr. Rela Institute and Medical Center, India (virtual)

Short Break

Serum bile acid control in maralixibat-treated patients with PFIC due to BSEP deficiency is associated with transplant-free survival and improved health-related quality of life.
Dr. Loomes, Children’s Hospital Philadelphia (in person)

Predicting Autoimmunity Post Gene Therapy
Dr. Aki Asai, Cincinnati Children’s Medical Center (in person)

Break

Working Lunch & Roundtable 2 (on location lunch buffet)
Discussion Related to “Treatment Development”

Conference Close: Bringing Hope to the Community
Walter Perez, Parent, President of PFIC Network

Hors D’eurves & Cocktail Hour

Dinner, Reception; on location dinner provided