Day 1 Agenda

PFIC Network Scientific Conference 2022 Agenda

April 29-30 in Pittsburgh, PA and virtual
*Agenda is subject to changes*

Day 1:

8:00 – 8:15

8:15 – 8:30

8:30 – 9:00

9:00 – 9:45

9:45 – 10:30

10:30 – 11:00

Friday, April 29th

Welcome Address: A Parent’s Story
Emily Ventura, on behalf of an anonymous caregiver (in person)

Presenting: The PFIC Network Patient Registry
Dr. Gitta Lubke, PFIC Network Research Strategist (in person)

The Spectrum of Genetic Cholestasis Syndromes: The Origin of FIC
Dr. Richard Thompson, Kings College London (virtual)

Introduction to ChiLDReN Network
Dr. Ben Shneider, Texas Children’s Hospital
Dr. Ron Sokol, Children’s Hospital Colorado (virtual)

Introduction to the NAPPED Consortium
Dr. Henkjan Verkade, University Medical Center, Groninden, Netherlands (in person)

Short Break (morning snack provided)

Scientific Presentations: Block #1
20 Minute Presentations + 10 Minute Q&A

Moderated by Dr. Ben Shneider, Texas Children’s Hospital

11:00 – 11:30

11:30 – 12:00

12:00 – 12:30

12:30 – 1:30

Roundtable Discussions
Moderated by Dr. James Squires,
Children’s Hospital Pittsburgh

1:30 – 3:30

3:30 – 4:00

4:00 – 5:00

Advances in Dissecting the Molecular Genetics of PFIC
Dr. Chunyue Yin, Cincinnati Children’s Medical Center (in person)

Modeling PFIC 1 Using Patient-Specific Stem Cells
Dr. Rodrigo Florentino, University of Pittsburgh (in person)

Effects on Serum Bile Acids, Pruritus, and Safety With Up to 72 Weeks of Odevixibat Treatment: Pooled Data From the PEDFIC 1 and PEDFIC 2 Studies in Children With Progressive Familial Intrahepatic Cholestasis
Dr. Henkjan Verkade, University Medical Center, Groningen, Netherlands (in person)

Lunch Break; on location lunch buffet for all participants
Activity: Kids ask questions to providers

Q&A and Roundtable 1
Discussion related to “Current Management Pathways”

Short Break

Community Keynote: Family Stories from Around the Globe
Zunera Dilshad, PFIC Parent, Pakistan
Francesca Lombardozzi, PFIC Parent, PFIC Itilia Network, Italy
Bernadetta Skora, PFIC Parent, PFIC Network Polska, Malta, Poland